Bibliotecas PUC-SP - Busca Integrada

Assessing the value of orphan drugs using conventional cost-effectiveness analysis: Is it fit for purpose?

Por Maarten J. Postma, Declan Noone, Mark H. Rozenbaum, John A. Carter, Marc F. Botteman, Elisabeth Fenwick, Louis P. Garrison
Publicado no Orphanet Journal of Rare Diseases (2022-04-01)

Recombinant factor IX‐Fc fusion protein in severe hemophilia B: Patient‐reported outcomes and health‐related quality of life

Por Mairead O’Donovan, Eimear Quinn, Kate Johnston, Evelyn Singleton, Julie Benson, Brian O'Mahony, Declan Noone, Cleona Duggan, Ruth Gilmore, Kevin Ryan, James S. O'Donnell, Niamh M. O’Connell
Publicado no Research and Practice in Thrombosis and Haemostasis (2021-10-01)